KEGG   DRUG: Cerliponase alfa
Entry
D10813                      Drug                                   
Name
Cerliponase alfa (USAN/INN);
Cerliponase alfa (genetical recombination) (JAN);
Brineura (TN)
Product
Sequence
SYSPEPDQRR TLPPGWVSLG RADPEEELSL TFALRQQNVE RLSELVQAVS DPSSPQYGKY
LTLENVADLV RPSPLTLHTV QKWLLAAGAQ KCHSVITQDF LTCWLSIRQA ELLLPGAEFH
HYVGGPTETH VVRSPHPYQL PQALAPHVDF VGGLHRFPPT SSLRQRPEPQ VTGTVGLHLG
VTPSVIRKRY NLTSQDVGSG TSNNSQACAQ FLEQYFHDSD LAQFMRLFGG NFAHQASVAR
VVGQQGRGRA GIEASLDVQY LMSAGANIST WVYSSPGRHE GQEPFLQWLM LLSNESALPH
VHTVSYGDDE DSLSSAYIQR VNTELMKAAA RGLTLLFASG DSGAGCWSVS GRHQFRPTFP
ASSPYVTTVG GTSFQEPFLI TNEIVDYISG GGFSNVFPRP SYQEEAVTKF LSSSPHLPPS
SYFNASGRAY PDVAALSDGY WVVSNRVPIP WVSGTSASTP VFGGILSLIN EHRILSGRPP
LGFLNPRLYQ QHGAGLFDVT RGCHESCLDE EVEGQGFCSG PGWDPVTGWG TPNFPALLKT
LLNP
(Disulfide bridge: 92-103, 346-507, 503-518)
  Type
Peptide
Remark
Therapeutic category: 3959
ATC code: A16AB17
Product: D10813<JP/US>
Efficacy
Lysosomal storage disease treatment, Enzyme replacement (tripeptidyl peptidase)
  Disease
Neuronal ceroid lipofuscinosis type 2 [DS:H00149]
  Type
Enzyme replacement therapy product
Target
TPP1* [HSA_VAR:1200v1] [HSA:1200] [KO:K01279]
  Pathway
hsa04142  Lysosome
Brite
Anatomical Therapeutic Chemical (ATC) classification [BR:br08303]
 A ALIMENTARY TRACT AND METABOLISM
  A16 OTHER ALIMENTARY TRACT AND METABOLISM PRODUCTS
   A16A OTHER ALIMENTARY TRACT AND METABOLISM PRODUCTS
    A16AB Enzymes
     A16AB17 Cerliponase alfa
      D10813  Cerliponase alfa (USAN/INN) <JP/US>
USP drug classification [BR:br08302]
 Genetic, Enzyme, or Protein Disorder: Replacement, Modifiers, Treatment
  Cerliponase alfa
   D10813  Cerliponase alfa (USAN/INN)
Therapeutic category of drugs in Japan [BR:br08301]
 3  Agents affecting metabolism
  39  Other agents affecting metabolism
   395  Enzyme preparations
    3959  Others
     D10813  Cerliponase alfa (USAN/INN); Cerliponase alfa (genetical recombination) (JAN)
Target-based classification of drugs [BR:br08310]
 Enzymes
  Hydrolases (EC3)
   Peptidyl-peptidases
    TPP1* [HSA_VAR:1200v1]
     D10813  Cerliponase alfa (USAN/INN) <JP/US>
New drug approvals in the USA [br08319.html]
 New molecular entities and new therapeutic biological products
  D10813
New drug approvals in Europe [br08329.html]
 European public assessment reports (EPAR) authorised medicine
  D10813
New drug approvals in Japan [br08318.html]
 Drugs with new active ingredients
  D10813
New drug approvals in the USA, Europe and Japan [br08328.html]
 Approval dates by FDA, EMA and PMDA
  D10813
Pharmacogenomic biomarkers [br08341.html]
 Germline mutations in genetic disorder treatments
  D10813
Other DBs
CAS: 151662-36-1
PubChem: 319902614
LinkDB

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