KEGG   DRUG: Atidarsagene autotemcel
Entry
D12877                      Drug                                   
Name
Atidarsagene autotemcel (USAN/INN);
Lenmeldy (TN)
Product
LENMELDY (Orchard Therapeutics (Europe))
Remark
ATC code: A16AB21
Product: D12877<US>
Efficacy
Methabolic disease therapeutic agent
  Disease
Metachromatic leukodystrophy [DS:H00127]
  Type
Cellular therapy product
Comment
Treatment of Metachromatic Leukodystrophy
Target
ARSA [HSA:410] [KO:K01134]
CD34 [HSA:947] [KO:K06474]
  Pathway
hsa04142  Lysosome
hsa04514  Cell adhesion molecule (CAM) interaction
hsa04640  Hematopoietic cell lineage
Brite
Anatomical Therapeutic Chemical (ATC) classification [BR:br08303]
 A ALIMENTARY TRACT AND METABOLISM
  A16 OTHER ALIMENTARY TRACT AND METABOLISM PRODUCTS
   A16A OTHER ALIMENTARY TRACT AND METABOLISM PRODUCTS
    A16AB Enzymes
     A16AB21 Atidarsagene autotemcel
      D12877  Atidarsagene autotemcel (USAN/INN) <US>
Target-based classification of drugs [BR:br08310]
 Cell surface molecules and ligands
  Other cell surface molecules
   CD molecules
    CD34
     D12877  Atidarsagene autotemcel (USAN/INN) <US>
 Enzymes
  Hydrolases (EC3)
   Sulfatases
    ARSA
     D12877  Atidarsagene autotemcel (USAN/INN) <US>
New drug approvals in the USA [br08319.html]
 Cellular and gene therapy products
  D12877
New drug approvals in the USA, Europe and Japan [br08328.html]
 Approval dates by FDA, EMA and PMDA
  D12877
Other DBs
PubChem: 497621290
LinkDB

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