NETWORK: N10017
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Entry
N10017 Network
Name
Replacement of deficient GBA
Definition
(Imiglucerase,
Velaglucerase,
Taliglucerase) -> GBA*
Expanded
(D03020,
D09029,
D09675) -> 2629v1
Type
Drug target
Gene
2629
GBA; glucosylceramidase beta
Variant
2629v1
GBA deficiency
Perturbant
D03020
Imiglucerase
D09029
Velaglucerase alfa
D09675
Taliglucerase alfa
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