KEGG   DRUG: Viltolarsen
Entry
D11528                      Drug                                   

Name
Viltolarsen (JAN/USAN);
Viltepso (TN)
Product
Formula
C244H381N113O88P20
Exact mass
6921.3564
Mol weight
6924.8155
Remark
Therapeutic category: 1900
Product: D11528<JP/US>
Efficacy
Translation inhibitor
  Disease
Duchenne muscular dystrophy (amenable to exon 53 skipping mutated) [DS:H01963]
Comment
Antisense oligonucleotide
Treatment of Duchenne muscular dystrophy
Target
DMD* [HSA_VAR:1756v1] [HSA:1756] [KO:K10366] (pre-mRNA exon53)
Brite
Therapeutic category of drugs in Japan [BR:br08301]
 1  Agents affecting nervous system and sensory organs
  19  Other agents affecting nervous system and sensory organs
   190  Other agents affecting nervous system and sensory organs
    1900  Other agents affecting nervous system and sensory organs
     D11528  Viltolarsen (JAN/USAN)
Target-based classification of drugs [BR:br08310]
 Not elsewhere classified
  Cellular process
   Cytoskeleton
    DMD* [HSA_VAR:1756v1]
     D11528  Viltolarsen (JAN/USAN) <JP/US>
New drug approvals in the USA [br08319.html]
 New molecular entities and new therapeutic biological products
  D11528
New drug approvals in Japan [br08318.html]
 Drugs with new active ingredients
  D11528
New drug approvals in the USA, Europe and Japan [br08328.html]
 Approval dates by FDA, EMA and PMDA
  D11528
Pharmacogenomic biomarkers [br08341.html]
 Germline mutations in genetic disorder treatments
  D11528
Other DBs
CAS: 2055732-84-6
PubChem: 384585504
LinkDB

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