KEGG   DRUG: Golodirsen
Entry
D11707                      Drug                                   

Name
Golodirsen (USAN/INN);
Vyondys 53 (TN)
Product
Formula
C305H481N138O112P25
Exact mass
8642.9625
Mol weight
8647.2841
Remark
Product: D11707<US>
Efficacy
Translation inhibitor
  Disease
Duchenne muscular dystrophy (DMD variant amenable to exon 53 skipping) [DS:H01963]
Comment
Antisense oligonucleotide
Target
DMD* [HSA_VAR:1756v1] [HSA:1756] [KO:K10366]
Brite
Target-based classification of drugs [BR:br08310]
 Not elsewhere classified
  Cellular process
   Cytoskeleton
    DMD* [HSA_VAR:1756v1]
     D11707  Golodirsen (USAN/INN) <US>
New drug approvals in the USA [br08319.html]
 New molecular entities and new therapeutic biological products
  D11707
New drug approvals in the USA, Europe and Japan [br08328.html]
 Approval dates by FDA, EMA and PMDA
  D11707
Pharmacogenomic biomarkers [br08341.html]
 Germline mutations in genetic disorder treatments
  D11707
Other DBs
CAS: 1422959-91-8
PubChem: 405226573
LinkDB

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