KEGG   DRUG: Brogidirsen
Entry
D12966                      Drug                                   
Name
Brogidirsen (JAN/USAN/INN)
Formula
C280H440N119O105P23
Exact mass
7861.6714
Mol weight
7865.63
Efficacy
Translation inhibitor
  Type
Antisense oligonucleotide
Comment
Treatment of Duchenne muscular dystrophy
Target
DMD [HSA:1756] [KO:K10366] (pre-mRNA exon44)
Brite
Target-based classification of drugs [BR:br08310]
 Not elsewhere classified
  Cellular process
   Cytoskeleton
    DMD
     D12966  Brogidirsen (JAN/USAN/INN)
Other DBs
CAS: 2409088-11-3
PubChem: 503268986
LinkDB

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