KEGG   DRUG: Zeleciment
Entry
D13112                      Drug                                   
Name
Zeleciment (USAN/INN)
Formula
C2122H3272N562O685S11
Exact mass
47939.5404
Mol weight
47968.77
Sequence
(Heavy chain)
QVQLQESGPG LVKPSQTLSL TCTVTGYSIT SGYYWNWIRQ PPGKGLEWIG YITFDGANNY
NPSLKNRVSI SRDTSKNQFS LKLSSVTAED TATYYCTRSS YDYDVLDYWG QGTTVTVSSA
STKGPSVFPL APSSKSTSGG TAALGCLVKD YFPEPVTVSW NSGALTSGVH TFPAVLQSSG
LYSLSSVVTV PSSSLGTQTY ICNVNHKPSN TKVDKKVEPK SCDKTHT
(Light chain)
DIQMTQSPSS LSASVGDRVT ITCRASQDIS NFLNWYQQKP GQPVKLLIYY TSRLHSGVPS
RFSGSGSGTD FTLTISSLQP EDFATYYCQQ GHTLPYTFGQ GTKLEIKRTV AAPSVFIFPP
SDEQLKSGTA SVVCLLNNFY PREAKVQWKV DNALQSGNSQ ESVTEQDSKD STYSLSSTLT
LSKADYEKHK VYACEVTHQG LSSPVTKSFN RGEC
(Disulfide bridge: H22-H96, H146-H202, H222-L214, L23-L88, L134-L194)
  Type
Peptide
Efficacy
Restoring or replacing dystrophin
  Type
Monoclonal antibody
Comment
Treatment of Duchenne muscular dystrophy
Target
TFRC (CD71) [HSA:7037] [KO:K06503]
  Pathway
hsa04350  TGF-beta signaling pathway
Brite
Target-based classification of drugs [BR:br08310]
 Peptidases and inhibitors
  Metallo peptidases
   Family M28
    TFRC (CD71)
     D13112  Zeleciment (USAN/INN)
Other DBs
CAS: 2725863-34-1
PubChem: 508750782
LinkDB

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