NETWORK: N10016
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Entry
N10016 Network
Name
Pharmacological chaperone of amenable GLA mutation
Definition
Migalastat -> GLA*
Expanded
D05031 -> 2717v2
Type
Drug target
Gene
2717
GLA; galactosidase alpha
Variant
2717v2
GLA mutation, migalastat amenable
Perturbant
D05031
Migalastat hydrochloride
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