KEGG   DRUG: Vutrisiran
Entry
D11917                      Drug                                   
Name
Vutrisiran (USAN/INN)
Formula
C530H715F9N171O323P43S6
Exact mass
16336.1678
Mol weight
16344.56
Remark
ATC code: N07XX18
Chemical structure group: DG03127
Product (DG03127): D11916<JP/US>
Efficacy
Gene expression regulator
  Type
RNA interference (RNAi) drug
Comment
Treatment of transthyretin (TTR)-mediated amyloidosis (ATTR amyloidosis)
Target
TTR [HSA:7276] [KO:K20731] (mRNA)
  Pathway
hsa04918  Thyroid hormone synthesis
Brite
Anatomical Therapeutic Chemical (ATC) classification [BR:br08303]
 N NERVOUS SYSTEM
  N07 OTHER NERVOUS SYSTEM DRUGS
   N07X OTHER NERVOUS SYSTEM DRUGS
    N07XX Other nervous system drugs
     N07XX18 Vutrisiran
      D11917  Vutrisiran (USAN/INN)
Target-based classification of drugs [BR:br08310]
 Transporters
  Other transporters
   Others
    TTR
     D11917  Vutrisiran (USAN/INN)
Other DBs
CAS: 1867157-35-4
PubChem: 497620330
LinkDB

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