KEGG   DRUG: Lunsotogene parvec
Entry
D13347                      Drug                                   
Name
Lunsotogene parvec (USAN/INN);
Lunsotogene parvec-cwha;
Otarmeni (TN)
Efficacy
Otoferlin production promotor
  Disease
Sensorineural hearing loss (molecularly confirmed biallelic variants in the OTOF gene) [DS:H00605]
  Type
Gene therapy product
Comment
Treatment of OTOF-related congenital hearing loss due to congenital auditory neuropathy
Target
OTOF [HSA:9381] [KO:K19949]
Brite
New drug approvals in the USA [br08319.html]
 Cellular and gene therapy products
  D13347
New drug approvals in the USA, Europe and Japan [br08328.html]
 Approval dates by FDA, EMA and PMDA
  D13347
Other DBs
CAS: 2907748-12-1
LinkDB

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