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Entry Name Name(TN) Disease
D09916 Ivacaftor (USAN/INN) Kalydeco (TN) Cystic fibrosis (CFTR mutation) [DS:H00218]
D10685 Lumacaftor and ivacaftor Orkambi (TN) Cystic fibrosis (CFTR F508del homozygous mutation) [DS:H00218]
D11042 Tezacaftor and ivacaftor Symdeko (TN) Cystic fibrosis (CFTR F508del homozygous mutation) [DS:H00218]
Cystic fibrosis (at least one mutation in CFTR) [DS:H00218]
D11700 Elexacaftor, ivacaftor and tezacaftor Trikafta (TN)
Kaftrio (TN)
Cystic fibrosis (CFTR F508del mutation) [DS:H00218]
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